Gene therapy Myotonic Dystrophy type 1 DMD Nuclear envelope Cell therapy OPMD Glutamate Myopathy MBNL Long read sequencing Myogenesis Inflammation Spinal muscular atrophy Dynamin 2 Lamin A/C LMNA gene CTG repeat contractions Laminopathies Myositis Duchenne muscular dystrophy Laminopathie Myotonic dystrophy type 1 Regeneration Outcome measures RNA biology CMS Cardiomyopathy Cancer Rare diseases Mouse model Heart Astrocyte Antisense oligonucleotides Aged Motoneuron Centronuclear myopathy Mice Autoantibodies Autophagy Genotype phenotype correlation ALS Thérapie génique Becker muscular dystrophy Congenital myopathy Congenital muscular dystrophy COVID-19 Treatment Calcium Myotonic dystrophy Myasthenia gravis Muscle Transcriptomics Muscular dystrophy Thymus Aging Dystrophin Animals Actin Autoimmune diseases Neuromuscular junction Muscle regeneration FSHD Rare neuromuscular diseases Neuromuscular diseases Autoimmunity Myasthenia Gravis MG Biomarkers Satellite cell Trinucleotide repeat expansion Skeletal muscle Neuromuscular disease Biomarker Myopathies RNA interference Amyotrophic lateral sclerosis Fibrosis Humans Dermatomyositis Myotonic Dystrophy CRISPRi Exercise Transgenic mouse model Errance diagnostique AAV Brain Dilated cardiomyopathy Myoblasts PABPN1 Cytoskeleton Heart failure Fabry disease Laminopathy Therapy Male Satellite cells Lamin A/C LMNA Mechanotransduction Cytokines LMNA gene Alternative splicing